Trong các nghiên cứu lâm sàng, Casgevy được chứng minh giúp khôi phục hoạt động sản sinh hemoglobin khỏe mạnh ở đa số bệnh nhân mắc bệnh thiếu máu hồng cầu lưỡi liềm.
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