Nước đầu tiên cấp phép liệu pháp gene điều trị bệnh thiếu máu do di truyền
Trong các nghiên cứu lâm sàng, Casgevy được chứng minh giúp khôi phục hoạt động sản sinh hemoglobin khỏe mạnh ở đa số bệnh nhân mắc bệnh thiếu máu hồng cầu lưỡi liềm.
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lcOqeMO54bul4buncHjDquG7leG6uOG6qsOqduG7jXfDquG6rOG7iXjDueG6rcOq4buUw6zhuqzDueG7m+G7gOG7hMOqxqHDieG6tuG7lcOq4buV4bul4bq4eMO5w6p34buneOG7pcOqw7nhu6dCw4LDquG7r+G7pUHhu6fDqsOC4bulROG7lcOq4bulecSp4bqow6rGoeG6oHjDucOq4bqsanjDquG6rOG7p3jhu6XDquG7peG7m3d5w7l2eeG7meG7p3jDquG7r+G7peG7t+G7m8Oqd8SpeOG7pcOq4bqyw6rGocOsw6rhuqzDgcOq4buZc3jhu6XDqnjhu6Xhu414w6p3beG7lcOq4buZc3jhu6XDquG6qOG7peG7p3HhuqrDqnfhu4vhuqrDquG7pcOAeMO5w6rhu5XDteG6qsOqdsOJ4bq04bunw6p24buncnfDquG7gOG7icOq4buV4buL4buVw6rhu5lzeOG7pcOqeOG7peG7jXjDqndt4buVw6rOssOqLeG6qOG7pcOsdsOs4bqs4bqsw6zhu5t34bunw6zDqsOC4bulRMOq4bqo4bul4bqq4bqg4buVw6rhu4Dhu4l5w6rhuqjhuqbhuqrhu4RyeMOqd+G7i+G6quG6rcOqw7nhu6dCw4LDqsO54bunanfDquG7leG7i+G7lcOq4bqo4bqm4bunc+G6qsOq4buV4bul4bq4eMO5w6rhu5lzeOG7peG6qWQvw4LEkWTDgsOq4buVdsOs4bqs4bqs4bqv4bq9w4Lhu5h54buX4buE4bq9xJHhu67hu6VBeMO5w6rDguG7peG7i+G6qMOq4bul4bunc3jDqnjDueG6quG7hMOq4buVxILDqsah4buLeMO5w6rhu690w6rhuqjhuqZ5eMO5w6rhu5Xhu4vhu5XDquG6qOG7pcOKw6p4w7nhu6Xhu6dzd+G6qcOq4buUxILDquG6pOG6qsOseMOqeOG7ieG7hMOq4buVRXjDucOqxqFrw6rhuqjhu6Xhu5t5w6rhu5fhu7nhu6fDquG7leG7pW/huqjDquG7leG7peG7ocOqd+G6uOG7lcOqxqHhuqDDqsOseMOq4bqoeeG7iXjDquG7lcSQw6zDquG6qOG7peG6qsOB4buV4bqpZC/DgsSRZMOCw6rhu5V2w6zhuqzhuqzhuq/hur3DguG7mHnhu5fhu4Thur3EkT7hu6XhuqrDgeG7lcOq4buUw6zhuqzDueG7m+G7gOG7hMOqduG7j+G7hMOq4bqoccOq4buZ4buJecOqw7nDgeG7lcOq4bqo4bq6w6rhuqjEkOG7hMOq4buCw4nEgnjDucOq4buVxJDDrMOq4buZc3jhu6XDqnjhu6Xhu414w6rhu4Dhu4nDquG7leG7peG7q3jhu6XDquG6rMOKw6zDqnfhuqDhuqjDqsO54bubeOG7m8Oq4bqo4bqmeXjDucOq4buV4buL4buVw6rhuqhxw6rhu5nhu4l5w6rDucOB4buVw6rhuqjhuqZ5eMO5w6rDguG7peG7s3jDucOq4bqo4bulxanDqnjDueG7peG7p3N34bqpZC/DgsSRZMOCw6rhu5V2w6zhuqzhuqzhuq/hur3DguG7mHnhu5fhu4Thur3EkeG7lOG7i+G7lcOq4bqoccOq4buZ4buJecOq4bqsw6zhuqrDquG7r+G7peG7p8OqxqHDieG6tuG7lcOq4buV4bul4bureOG7pcOq4bqsw4rDrMOq4bqs4buhw6rGocOJ4bq24buVw6rhuqjhuqbhuqrhu4RyeMOq4bqo4bqm4bqyw6p2xKnhu6fDquG7gOG7iXnDquG7lcSCw6rhuqjhu6V0w6rhu5lzeOG7pcOqeOG7peG7jXjDquG7gOG6ruG7p8OqxqHhu6dy4bqqw6rhu6/hu6dzeMOq4buZc3jhu6XDqnjhu6Xhu414w6rGoWvDquG6qOG6pmrhu6fDquG6pOG6qsOsw6rhuqThuqrhu4vDquG6qOG6psaweOG7pcOqxqHhu6dy4bqqw6rhuqjhuqbhu6nDqsah4bunw6rhu6/DqHfDqsahdMOq4bqoxJDhu4TDquG7gsOJxIJ4w7nDquG6rMOyeMOq4bqs4buJeMO5w6rhuqjhu6dxw4LDqnjhu6XDtHjDquG6qHHDquG7meG7iXnDqsahw4nhurbhu5XDquG6qOG6puG6quG7hHJ4w6rhu4Dhu4l54bqpZC/DgsSRZMOCw6rhu5V2w6zhuqzhuqzhuq/hur3DguG7mHnhu5fhu4Thur3EkT7hu6XhuqrDgeG7lcOq4buXecOqNuG7m+G6puG6qOG7m+G7gsOqIeG7pcOs4bqmd8Os4buV4bub4bqq4bqo4bun4buVw6x24bqsw6rhu4Dhu4nDquG7lCnhu6Y8ISnDqj7hu6Xhu5vhuqbDrMOC4bub4bqq4bqo4bun4buV4bqsw6rDguG7pcOB4bunw6rhu6XhurbDgsOqw4Lhu6Xhu4vhuqjDquG6qOG6puG7p3R4w6rhu4Dhu4nDquG6rGp4w6rhu4Lhuqrhu4/huqjhuqkv4bqpZC/DgsSRZMOCw6rhu5V2w6zhuqzhuqzhuq/hur3DguG7mHnhu5fhu4Thur3DquG6rOG6qOG7hHbhu5vhuq/hur3huqjhu5vhu4Lhuqgtw6x24bunw7l44bqlw6rhuqbhu6fDueG7peG6qOG6p+G6vcSRPuG7peG7m3nDqj4+ODZYZC/DgsSR