Nước đầu tiên cấp phép liệu pháp gene điều trị bệnh thiếu máu do di truyền
Trong các nghiên cứu lâm sàng, Casgevy được chứng minh giúp khôi phục hoạt động sản sinh hemoglobin khỏe mạnh ở đa số bệnh nhân mắc bệnh thiếu máu hồng cầu lưỡi liềm.
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4bqt4buvw6Fmc+G7l27DoeG7reG6qeG7l8Oh4butw7Phu5dvw6FvZ+G7lcahbuG7mcah4buHw7Phu5fDoeG7k2/hu59nw6Hhu5Xhuq3hu5dvw6HFqcOhZsOiw6Hhu61xw6Hhu4dq4buXb8Oh4buXb+G6ueG7l8Oh4buVY+G7g8Oh4buHauG7l2/DoeG7r2/Ds+G7iXbDoeG7leG6pXbDoW9y4buXbsOh4buD4bq9dsOh4buZ4bu1xrDDs8Oh4buZw7PEqeG7lcOh4bqg4bqnw6Hhu4PhuqXhu4PDoeG7h2rhu5dvw6Hhu5dv4bq54buXw6Hhu5Vj4buDw6HOssOhLeG7r2/DouG7mcOi4but4butw6Jn4buVw7PDosOh4bupb3nDoeG7r292c+G7g8Oh4bqg4bqnxqHDoeG7r+G7sXbEgsSp4buXw6Hhu5XhuqV2IMOhbsOzd+G7qcOhbsOz4bqp4buVw6Hhu4PhuqXhu4PDoeG7r+G7scOzanbDoeG7g2/hu7fhu5duw6Hhu4dq4buXbzA0L+G7qTU04bupw6Hhu4Phu5nDouG7reG7rSlh4bup4buGxqHhu4XEgmE14buSb3Dhu5duw6Hhu6lv4bql4buvw6Fvw7Nq4buXw6Hhu5dudsSCw6Hhu4PDusOhZuG6peG7l27DoeG7k2vDoeG7r+G7scah4buXbsOh4buD4bql4buDw6Hhu69vw4HDoeG7l25vw7Nq4buVMMOh4buCw7rDoeG7q3bDouG7l8Oh4buX4bqnxILDoeG7g+G7s+G7l27DoWbhuqvDoeG7r29nxqHDoeG7heG7ocOzw6Hhu4NvxJHhu6/DoeG7g2/DrMOh4buV4bu34buDw6Fmc8Ohw6Lhu5fDoeG7r8ah4bqn4buXw6Hhu4PDvcOiw6Hhu69vdnHhu4MwNC/hu6k1NOG7qcOh4buD4buZw6Lhu63hu60pYeG7qeG7hsah4buFxIJhNeG7rm92ceG7g8Oh4buCw6Lhu61uZ+G6oMSCw6Hhu5nhurvEgsOh4buv4buJw6Hhu4fhuqfGocOhbnHhu4PDoeG7r+G7ucOh4buvw73EgsOhw4Phu7XDuuG7l27DoeG7g8O9w6LDoeG7h2rhu5dvw6Hhu5dv4bq54buXw6HhuqDhuqfDoeG7g2/DteG7l2/DoeG7rcOBw6LDoeG7lXPhu6/DoW5n4buXZ8Oh4buv4buxxqHhu5duw6Hhu4PhuqXhu4PDoeG7r+G7icOh4buH4bqnxqHDoW5x4buDw6Hhu6/hu7HGoeG7l27DoeG7qW/hu53hu5duw6Hhu69vw7LDoeG7l25vw7Nq4buVMDQv4bupNTThu6nDoeG7g+G7mcOi4but4butKWHhu6nhu4bGoeG7hcSCYTXhu4LhuqXhu4PDoeG7r+G7icOh4buH4bqnxqHDoeG7rcOidsOh4buTb8Ozw6Fm4bu14bun4buDw6Hhu4Nvw7Xhu5dvw6Hhu63DgcOiw6Hhu63DrMOhZuG7teG7p+G7g8Oh4buv4buxdsSCxKnhu5fDoeG7r+G7scWpw6Hhu5nhuq3Ds8Oh4bqg4bqnxqHDoeG7g8O6w6Hhu69va8Oh4buHauG7l2/DoeG7l2/hurnhu5fDoeG6oMO5w7PDoWbDs8SpdsOh4buTw7Nq4buXw6Hhu4dq4buXb8Oh4buXb+G6ueG7l8OhZuG6q8Oh4buv4bux4bqpw7PDoeG7q3bDosOh4burduG6pcOh4buv4bux4buN4buXb8OhZsOzxKl2w6Hhu6/hu7Hhu4/DoWbDs8Oh4buTw6jhu5XDoWZrw6Hhu6/DvcSCw6HDg+G7tcO64buXbsOh4butw6nhu5fDoeG7reG6p+G7l27DoeG7r8Oz4buJ4bupw6Hhu5dvw6rhu5fDoeG7r+G7icOh4buH4bqnxqHDoWbhu7Xhu6fhu4PDoeG7r+G7sXbEgsSp4buXw6HhuqDhuqfGoTA0L+G7qTU04bupw6Hhu4Phu5nDouG7reG7rSlh4bup4buGxqHhu4XEgmE14buub3Zx4buDw6Hhu4XGocOhJGfhu7Hhu69nw4PDoeG7qG/DouG7seG7lcOi4buDZ3bhu6/Ds+G7g8Oi4buZ4butw6HhuqDhuqfDoeG7guG7sMOT4bus4buo4buww6Hhu65vZ+G7scOi4bupZ3bhu6/Ds+G7g+G7rcOh4bupb3HDs8Ohb+G7p+G7qcOh4bupb+G6peG7r8Oh4buv4buxw7Nr4buXw6HhuqDhuqfDoeG7reG6qeG7l8Ohw4N24bq74buvMC8wNC/hu6k1NOG7qcOh4buD4buZw6Lhu63hu60pYeG7qeG7hsah4buFxIJhw6Hhu63hu6/EguG7mWcpYeG7r2fDg+G7ry3DouG7mcOzbuG7l13DoeG7scOzbm/hu68iYTXhu65vZ8ahw6Hhu67hu64qJOG7ljQv4bupNQ==