Bệnh nhân đầu tiên được điều trị bằng kỹ thuật chỉnh sửa gene cá nhân hóa
Một trẻ sơ sinh người Mỹ, mắc căn bệnh hiếm gặp, đã trở thành bệnh nhân đầu tiên trong lịch sử được điều trị bằng kỹ thuật chỉnh sửa gene cá nhân hóa. Điều này mở ra hy vọng tươi sáng cho những người mắc các bệnh hiếm gặp.
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